Lancashire and South Cumbria
Formulary
 
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9 Nutrition and blood

This chapter of the formulary is under continual development, please let the team know if you have any comments about the contents: mlcsu.lscformulary@nhs.net. 

For more information about the formulary development process, please see: https://www.lancsmmg.nhs.uk/lancashire-and-south-cumbria-icb-formulary-development/

09-08-01 Drugs used in metabolic disorders

Asfotase alfa Strensiq®
Formulary

Tertiary Centre

Solution for injection

100mg/ml, 40mg/ml
Link  NICE: Asfotase alfa for treating paediatric-onset hypophosphatasia

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Avalglucosidase alfa Nexviadyme®
Formulary

Powder for concentrate for solution for infusion 100mg - for treating Pompe disease - see link below
Link  NICE TA821: Avalglucosidase alfa for treating Pompe disease

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Pegunigalsidase alfa Elafbrio®
Formulary

For treating Fabry disease
Link  NICE TA915: Pegunigalsidase alfa for treating Fabry disease

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Vutrisiran Amvuttra®
Formulary

25mg solution for injection in pre-filled syringe

Red for NICE TA868 Vutrisiran for treating hereditary transthyretin-related amyloidosis
Link  NICE TA868: Vutrisiran for treating hereditary transthyretin-related amyloidosis

Red View adult BNF  View SPC online  View childrens BNF